Clinical trials in SMA

Promising new treatments for SMA continue to be developed. They need to be tested in clinical trials. The registry has been set up to speed the process of finding patients that fulfill the eligibility criteria for the trials.

When recruitment for an SMA trial starts in the UK, the UK SMA Patient Registry will be in touch with those on the registry to let them know about it.

You can also find the information about current SMA related trials on the TREAT-NMD website.

The most comprehensive online listing of trials is at where companies are obliged to provide details of their trials.

A useful overview of the current trials can also be found on the SMA UK website.